Gene-edited neural cell therapy - UCB
Latest Information Update: 04 Jun 2026
At a glance
- Originator Neurona Therapeutics
- Developer UCB
- Class Cell therapies; Gene therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Neurological disorders
Most Recent Events
- 02 Jun 2026 Neurona Therapeutics has been acquired and merged into UCB
- 29 Jul 2024 Early research in Neurological disorders in USA (Parenteral) (Neurona Therapeutics pipeline, July 2024)
- 20 Sep 2022 Neurona Therapeutics has patent protection entitled "Neural progenitor cell populations and their uses" in Japan