Research programme: Huntington's disease therapeutics - BPG Bio
Latest Information Update: 03 Dec 2024
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At a glance
- Originator BPG Bio
- Class
- Mechanism of Action Huntingtin protein expression inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Huntington's disease
Most Recent Events
- 06 Aug 2024 Preclinical trials in Huntington's disease in USA (unspecified route) prior to August 2024 (BPG Bio Pipeline, August 2024)