KLTO 202
Alternative Names: AAVmyo.desmin.s-KL; KLTO-202Latest Information Update: 28 Jul 2025
At a glance
- Originator Klotho Neurosciences
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis; Isaacs syndrome; Multiple sclerosis; Neuromuscular disorders
Most Recent Events
- 22 Jul 2025 Klotho Neurosciences and AAVnerGene agree to develop KLTO 202
- 10 Jul 2025 KLTO 202 receives Orphan Drug status for Amyotrophic lateral sclerosis in USA
- 04 Jul 2025 Preclinical trials in Amyotrophic lateral sclerosis in USA (Parenteral) before July 2025 (Klotho Neurosciences pipeline, July 2025)