BAH 243
Alternative Names: BAH-243; Lentiviral vector modified CD34+ hematopoietic stem cell therapy - Essen BiotechLatest Information Update: 06 Sep 2024
Price :
$50 *
At a glance
- Originator Essen BioTech
- Class Antianaemics; Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Beta(A-T87Q) globin replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Sickle cell anaemia
Most Recent Events
- 01 Aug 2024 Phase-I/II clinical trials in Sickle cell anaemia (In children, In adolescents, In adults, In the elderly) in China (IV) (NCT06399107)