Research programme: hepatolenticular degeneration gene therapies - Prime Medicine
Latest Information Update: 02 Sep 2024
At a glance
- Originator Prime Medicine
- Class Gene therapies
- Mechanism of Action Gene expression modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hepatolenticular degeneration
Most Recent Events
- 17 Aug 2024 Preclinical trials in Hepatolenticular degeneration in USA (Parenteral) prior to August 2024