Research programme: neuromuscular therapeutics - Prime Medicine
Latest Information Update: 02 Sep 2024
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At a glance
- Originator Prime Medicine
- Class Gene therapies
- Mechanism of Action Gene expression modulators; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Duchenne muscular dystrophy; Myotonic dystrophy; Oculopharyngeal muscular dystrophy
Most Recent Events
- 17 Aug 2024 Early research in Duchenne muscular dystrophy in USA (Parenteral) prior to August 2024 (Prime Medicine pipeline, August 2024)
- 17 Aug 2024 Early research in Myotonic dystrophy in USA (Parenteral) prior to August 2024 (Prime Medicine pipeline, August 2024)
- 17 Aug 2024 Early research in Oculopharyngeal muscular dystrophy in USA (Parenteral) prior to August 2024 (Prime Medicine pipeline, August 2024)