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MGX 001

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Drug Profile

MGX 001

Alternative Names: MGX-001 - Metagenomi Therapeutics; MGX001

Latest Information Update: 29 Jan 2026

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At a glance

  • Originator Metagenomi
  • Developer Metagenomi Therapeutics
  • Class Antihaemorrhagics; Gene therapies
  • Mechanism of Action Factor VII replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Haemophilia A

Most Recent Events

  • 12 Jan 2026 Metagenomi completes pre-IND meeting in fourth quarter of 2025
  • 12 Jan 2026 Metagenomi plans first in human study in 2027
  • 12 Nov 2025 Metagenomi plans pre-IND/ex-US regulatory meetings for Haemophilia A in fourth quarter of 2025

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