Research programme: charcot marie tooth disease therapeutics - MitoRx Therapeutics
Latest Information Update: 28 Jul 2026
At a glance
- Originator MitoRx Therapeutics
- Class Small molecules
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Charcot-Marie-Tooth disease
Most Recent Events
- 28 Jul 2026 Discontinued for Charcot-Marie-Tooth disease in United Kingdom (PO) before July 2026 (MitoRx Therapeutics pipeline, July 2026)
- 12 Sep 2024 Early research in Charcot-Marie-Tooth disease in United Kingdom (PO), prior to September 2024 (MitoRx Therapeutics pipeline, September 2024)