MC GYS1
Alternative Names: MC-GYS1Latest Information Update: 08 Oct 2024
At a glance
- Originator miRecule
- Class Antibodies; Drug conjugates; Immunoconjugates; RNA
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Glycogen storage disease
Most Recent Events
- 25 Sep 2024 miRecule has patent protection for RNA chemistry to develop RNA therapeutics prior to September 2024 (miRecule website; September 2024)
- 25 Sep 2024 Early research in Glycogen storage disease in USA (Parenteral) piror to September 2024 (miRecule pipeline; September 2024)