PTX 101 - Primera Therapeutics
Alternative Names: PTX-101 - Primera TherapeuticsLatest Information Update: 06 Jan 2025
Price :
$50 *
At a glance
- Originator Primera Therapeutics
- Class Gene therapies
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Mitochondrial disorders
Most Recent Events
- 15 Oct 2024 Preclinical trials in Mitochondrial disorders in USA (Parenteral), prior to December 2022 (Primera Therapeutics pipeline, October 2024)
- 15 Oct 2024 Primera Therapeutics plans a phase I trial for Mitochondrial disorders in 2026 (Primera Therapeutics pipeline, October 2024)
- 15 Oct 2024 Primera Therapeutics plans to submit IND application for Mitochondrial disease in 1H of 2025 (Primera Therapeutics pipeline, October 2024)