Fragile x syndrome - Aptadir Therapeutics
Latest Information Update: 16 Dec 2024
Price :
$50 *
At a glance
- Originator Aptadir Therapeutics
- Class RNA
- Mechanism of Action DNA cytosine 5 methyltransferase 1 inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Fragile X syndrome
Most Recent Events
- 23 Oct 2024 Early research in Fragile X syndrome in Italy (Parenteral), prior to October 2024 (Aptadir Therapeutics pipeline, October 2024)