RTY 694
Alternative Names: RTY-694Latest Information Update: 19 May 2025
At a glance
- Originator Rectify Pharma
- Class Small molecules
- Mechanism of Action ATP-binding cassette transporter modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Primary sclerosing cholangitis
Most Recent Events
- 09 May 2025 Pharmacodynamics data from a preclinical trial in Primary sclerosing cholangitis released by Rectify pharmaceuticals
- 18 Nov 2024 Pharmacodynamics data from a preclinical trial in Primary sclerosing cholangitis released by Rectify pharmaceuticals
- 18 Nov 2024 Rectify Pharmaceuticals plans a Clinical trial for Primary sclerosing cholangitis