ALN 6400
Alternative Names: ALN-6400Latest Information Update: 02 Dec 2025
At a glance
- Originator Alnylam Pharmaceuticals
- Class Small interfering RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I/II Blood coagulation disorders
Most Recent Events
- 12 Nov 2025 Phase-I/II clinical trials in Blood coagulation disorders (In volunteers) in USA (SC) (NCT06659640)
- 12 Nov 2025 Phase-I/II clinical trials in Blood coagulation disorders in Canada (SC) (NCT06659640)
- 12 Jan 2025 Alnylam Pharmaceuticals plans to submit Investigational New Drug (IND) applications by the end of 2025