LBR 2950
Alternative Names: LBR-2950Latest Information Update: 20 Mar 2025
At a glance
- Originator Libra Therapeutics
- Class Small molecules
- Mechanism of Action Autophagy stimulants; MCOLN1 protein modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Neurodegenerative disorders
Most Recent Events
- 20 Mar 2025 Libra Therapeutics plans a phase I trial for Neurodegenerative disorders (Libra Therapeutics pipeline, March 2025)
- 01 Nov 2024 Preclinical trials in Neurodegenerative disorders in USA (unspecified route)