LDLR targeted GalNAc-AIMer - WaVe life Sciences
Latest Information Update: 22 Jan 2025
At a glance
- Originator WaVe life Sciences
- Class Amines; Amino sugars; Antihyperlipidaemics; Drug conjugates; Oligonucleotides; Pyrrolidines
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Hyperlipoproteinaemia type II