WTX 245
Alternative Names: WTX-245Latest Information Update: 06 Feb 2025
At a glance
- Originator WaveBreak
- Class Antidementias; Small molecules
- Mechanism of Action TDP-43 protein inhibitors
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis; Frontotemporal dementia
Most Recent Events
- 06 Dec 2024 Preclinical trials in Amyotrophic lateral sclerosis in USA (unspecified route)
- 06 Dec 2024 Preclinical trials in Frontotemporal dementia in USA (unspecified route)
- 06 Dec 2024 Pharmacodynamics data from a preclinical trial in Amyotrophic lateral sclerosis and frontemporal dementia released by Wavebreak