Research programme: small molecule therapeutics - GSK/Rgenta Therapeutics
Latest Information Update: 18 Mar 2025
At a glance
- Originator GSK; Rgenta Therapeutics
- Developer Rgenta Therapeutics
- Class Antineoplastics; Small molecules
- Mechanism of Action RNA splicing modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Unspecified