BEAM 103
Alternative Names: BEAM-103Latest Information Update: 04 Feb 2025
At a glance
- Originator Beam Therapeutics
- Class Antianaemics; Monoclonal antibodies
- Mechanism of Action Proto-oncogene protein c-kit inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Beta-thalassaemia; Sickle cell anaemia
Most Recent Events
- 08 Dec 2024 Preclinical trials in Beta-thalassaemia in USA (Parenteral) prior to December 2024
- 08 Dec 2024 Preclinical trials in Sickle cell anaemia in USA (Parenteral) prior to December 2024
- 08 Dec 2024 Adverse events and pharmacodynamics data from a preclinical study in sickle cell disease and beta thalassemia released by Beam Therapeutics ,