Drug Profile

Research programme: STAC-BBB based therapeutics - Astellas Gene Therapies/SangamoTherapeutics

Latest Information Update: 01 Apr 2025

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At a glance

Originator Sangamo Therapeutics
Developer Astellas Gene Therapies; Sangamo Therapeutics
Class Proteins; Transcription factors
Mechanism of Action DNA-binding protein modulators; Genetic transcription modulators

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity No

31 Dec 2024 Preclinical trials in Neurological disorders in USA (Parenteral) prior to December 2024
19 Dec 2024 Astellas Gene Therapies and Sangamo Therapeutics enters into a licensing agreement for STAC-BBB to develop genomic medicines to treat certain neurodegenerative diseases
19 Dec 2024 Early research in Neurological disorders in USA (Parenteral)

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