Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

Apc 001

Next Previous
Drug Profile

Apc 001

Alternative Names: Apc-001

Latest Information Update: 05 Feb 2025

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Aptacure Therapeutics
  • Class Oligonucleotides
  • Mechanism of Action SOST protein inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - X-linked dominant hypophosphataemic rickets
  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical X-linked dominant hypophosphataemic rickets

Most Recent Events

  • 23 Dec 2024 Preclinical trials in X-linked dominant hypophosphataemic rickets in Hongkong (unspecified route) prior to December 2024
  • 23 Dec 2024 Apc 001 receives Orphan Drug status for X-linked dominant hypophosphataemic rickets in USA
  • 23 Dec 2024 Apc 001 receives Rare pediatric disease designation for X-linked dominant hypophosphataemic rickets in USA

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top