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SGT 212

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Drug Profile

SGT 212

Alternative Names: SGT-212

Latest Information Update: 28 Feb 2025

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At a glance

  • Originator Solid Biosciences; University of Pennsylvania
  • Class Gene therapies
  • Mechanism of Action Frataxin protein replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Friedreich's ataxia

Most Recent Events

  • 21 Jan 2025 SGT 212 receives Fast Track designation for Friedreich's ataxia [IV,Infusion] in USA
  • 14 Jan 2025 Phase-I/II clinical trials in Friedreich's ataxia (IV) (Solid Biosciences pipeline, January 2025)
  • 14 Jan 2025 Phase-I/II clinical trials in (Intracerebral) (Solid Biosciences pipeline, January 2025)

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