VSA 012
Alternative Names: VSA-012Latest Information Update: 16 Sep 2026
At a glance
- Originator Visirna Therapeutics
- Class Small interfering RNA
- Mechanism of Action Complement factor B inhibitors
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Paroxysmal nocturnal haemoglobinuria
Most Recent Events
- 16 Sep 2026 NCT07816237- added FE
- 16 Sep 2026 Visirna Therapeutics plans a phase III trial for Paroxysmal nocturnal haemoglobinuria (Treatment-naive) in China (SC) in October 2026 (NCT07816237)
- 06 Dec 2025 Phase-I clinical trials in Paroxysmal nocturnal haemoglobinuria (Treatment-naive) in China (SC) (NCT06848296)