Research programme: metabolic disorder therapeutics - CorrectSequence Therapeutics
Latest Information Update: 28 Feb 2025
At a glance
- Originator CorrectSequence Therapeutics
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Metabolic disorders
Most Recent Events
- 23 Jan 2025 Preclinical trials in Metabolic disorders in China (Parenteral), prior to January 2025 (CorrectSequence Therapeutics pipeline, January 2025)