Drug Profile

BPN 36964

Alternative Names: BPN-36964

Latest Information Update: 05 Mar 2025

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At a glance

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

Yes - Familial dysautonomia
New Molecular Entity Yes

22 Jan 2025 Preclinical trials in Familial dysautonomia in USA (PO)
22 Jan 2025 BPN 36964 receives Orphan Drug status for Familial dysautonomia in USA
22 Jan 2025 US FDA grants Rare Pediatric Disease Designation to BPN 36964 for the treatment of Familial dysautonomia

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