Research programme: RNA therapeutics - Averna Therapeutics
Alternative Names: RNA/lipid nanoparticle (LNP)-based genomic therapeuticsLatest Information Update: 21 Feb 2025
At a glance
- Originator Averna Therapeutics
- Class Antineoplastics; RNA
- Mechanism of Action Protein expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase Unknown Autoimmune disorders; Cancer; Inborn genetic disorders