TL 001
Alternative Names: TL-001Latest Information Update: 14 May 2026
At a glance
- Originator Telaria
- Class Gene therapies; Skin disorder therapies
- Mechanism of Action Collagen type VII replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Epidermolysis bullosa