NP 3021
Alternative Names: NP-3021Latest Information Update: 16 Mar 2025
At a glance
- Originator Novel Pharma
- Class Recombinant proteins
- Mechanism of Action Beta-galactosidase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical GM1 gangliosidosis
Most Recent Events
- 21 Feb 2025 Preclinical trials in GM1-gangliosidosis in South Korea (Intracerebral), Prior to February 2025 (Novel pharma pipeline, February 2025)