NP 3031
Alternative Names: NP-3031Latest Information Update: 16 Mar 2025
At a glance
- Originator Novel Pharma
- Class Recombinant proteins
- Mechanism of Action Galactosylceramidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Globoid cell leukodystrophy
Most Recent Events
- 21 Feb 2025 Preclinical trials in Globoid cell leukodystrophy in South Korea (Intracerebral), prior to February 2025 (Novel pharma pipeline, February 2025)