Muscle disorder therapy - Novel pharma
Alternative Names: SAM - Novel pharmaLatest Information Update: 16 Mar 2025
At a glance
- Originator Novel Pharma
- Class
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Spinal muscular atrophy
Most Recent Events
- 24 Feb 2025 Early research in Spinal muscular atrophy in South Korea (unspecified route), prior to February 2025 (Novel Pharma pipeline, February 2025)