RG 6797
Alternative Names: RG-6797; SPK-8011QQLatest Information Update: 25 Feb 2025
At a glance
- Originator Spark Therapeutics
- Class Antihaemorrhagics; Gene therapies
- Mechanism of Action Factor VIII replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase II Haemophilia A
Most Recent Events
- 25 Feb 2025 Phase-II clinical trials in Haemophilia A (Parenteral), prior to February 2025 (Roche pipeline, February 2025)