STOKE ASO 1
Alternative Names: STOKE-ASO-1Latest Information Update: 31 Mar 2025
At a glance
- Originator Stoke Therapeutics
- Developer ACADIA Pharmaceuticals
- Class Antisense oligonucleotides; Eye disorder therapies
- Mechanism of Action Methyl-CpG-binding protein 2 expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Rett syndrome
Most Recent Events
- 26 Feb 2025 Early research in Rett syndrome in USA (unspecified route) before February 2025 (ACADIA Pharmaceuticals pipeline, February 2025)