BEBT 507
Alternative Names: BEBT-507Latest Information Update: 13 Jun 2025
At a glance
- Originator BeBetter Med
- Class Antineoplastics; Small interfering RNA
- Mechanism of Action RNA interference; TMPRSS6 protein expression inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Haemochromatosis; Polycythaemia vera
Most Recent Events
- 05 Jun 2025 BeBetter Med plans a phase I trial for Polycythemia vera (Treatment-experienced) in China (SC, Injection) in June 2025 (NCT07012109)
- 04 Mar 2025 Phase-I clinical trials in Haemochromatosis in China (Parenteral) before March 2025 (BeBetter Med pipeline, March 2025)
- 04 Mar 2025 Phase-I clinical trials in Polycythaemia vera in China (Parenteral) before March 2025 (BeBetter Med pipeline, March 2025)