Research programme: ACVR1C-targeted obesity therapeutics - Alnylam Pharmaceuticals
Latest Information Update: 31 Mar 2025
At a glance
- Originator Alnylam Pharmaceuticals
- Class Obesity therapies; Small interfering RNA
- Mechanism of Action ACVR1C protein expression inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Obesity