Research programme: toxic protein aggregate modifier - Remix therapeutics
Latest Information Update: 28 Mar 2025
At a glance
- Originator Remix Therapeutics
- Class Small molecules
- Mechanism of Action RNA modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Neurodegenerative disorders
Most Recent Events
- 12 Mar 2025 New profile created from (Remix Therapeutics pipeline, March 2025)
- 12 Mar 2025 Preclinical trials in Neurodegenerative disorders in USA (unspecified route) (Remix Therapeutics pipeline, March 2025)