RIG 301
Alternative Names: RIG-301Latest Information Update: 11 Apr 2025
At a glance
- Originator RIGImmune
- Class Antifibrotics; RNA
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cystic fibrosis
Most Recent Events
- 13 Mar 2025 RIGImmune plans a phase Ib proof of concept clinical trial for Cystic fibrosis in mid 2027 (Inhalation)
- 13 Mar 2025 Preclinical trials in Cystic fibrosis in USA (Inhalation), prior to July 2024 (RIGImmune pipeline, March 2025)
- 31 Jul 2024 Pharmacodynamics data from a preclinical trial in cystic fibrosis released by RIGImmune