SLN 548
Alternative Names: SLN-548Latest Information Update: 31 Mar 2025
At a glance
- Originator Silence Therapeutics
- Class Amino sugars; Drug conjugates; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Immunological disorders