AOC 1045
Alternative Names: AOC-1045Latest Information Update: 31 Mar 2025
At a glance
- Originator Avidity Biosciences
- Class Drug conjugates; Immunoconjugates; Monoclonal antibodies; Oligonucleotides; Small interfering RNA
- Mechanism of Action Dystrophin expression stimulants; RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 17 Mar 2025 AOC 1045 is available for licensing as of 17 Mar 2025. https://www.aviditybiosciences.com/pipeline/collaborations-and-partnerships/
- 17 Mar 2025 Preclinical trials in Duchenne muscular dystrophy in USA (unspecified route)