Research programme: neuromuscular disease therapeutics - Avidity Biosciences
Alternative Names: Rare neuromuscular disease therapeutics - Avidity BiosciencesLatest Information Update: 31 Mar 2025
At a glance
- Originator Avidity Biosciences
- Class Drug conjugates; Immunoconjugates; Monoclonal antibodies; Oligonucleotides; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Neuromuscular disorders
Most Recent Events
- 17 Mar 2025 Research programme: neuromuscular disease therapeutics - Avidity Biosciences is available for licensing as of 17 Mar 2025. https://www.aviditybiosciences.com/pipeline/collaborations-and-partnerships/
- 17 Mar 2025 Preclinical trials in Neuromuscular disorders in USA (unspecified route) (Avidity Biosciences pipeline, March,