Ultrasound mediated nonviral gene therapy - SonoThera
Latest Information Update: 16 Jan 2026
At a glance
- Originator SonoThera
- Class Gene therapies
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 08 Jan 2026 Pharmacodynamics data from a preclinical data from Duchenne muscular dystrophy released by SonoThera
- 08 Jan 2026 SonoThera plans a phase I trial for Duchenne muscular dystrophy in early 2027
- 08 Oct 2025 Pharmacodynamics data from a preclinical data from Duchenne muscular dystrophy released by SonoThera