TVR 110
Alternative Names: TVR-110Latest Information Update: 31 Mar 2025
At a glance
- Originator Armatus Bio
- Class Gene therapies; MicroRNAs
- Mechanism of Action Gene transference; PMP22 protein expression inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Charcot-Marie-Tooth disease
Most Recent Events
- 20 Mar 2025 Preclinical trials in Charcot-Marie-Tooth disease in USA (Intrathecal) (Armatus Bio pipeline, March 2025)