Research programme: C9orf72 RAN translation inhibitors - Libra Therapeutics
Latest Information Update: 25 Mar 2025
At a glance
- Originator Libra Therapeutics
- Class Antidementias; Small molecules
- Mechanism of Action Translational protein modification modulator
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Neurodegenerative disorders
Most Recent Events
- 20 Mar 2025 Early research in Neurodegenerative disorders in USA (unspecified route), before March 2025 (Libra Therapeutics pipeline, March 2025)