Research programme: respiratory gene therapies - Krystal Biotech
Latest Information Update: 01 Apr 2025
At a glance
- Originator Krystal Biotech
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Respiration disorders
Most Recent Events
- 21 Mar 2025 Preclinical trials in Respiration disorders in USA (Parenteral) (Krystal Biotech pipeline, March 2025)