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SAR 446268

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Drug Profile

SAR 446268

Alternative Names: SAR-446268

Latest Information Update: 31 Mar 2025

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At a glance

  • Originator Sanofi
  • Class Gene therapies
  • Mechanism of Action Gene transference; Myotonin protein kinase inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Myotonic dystrophy

Most Recent Events

  • 25 Mar 2025 Preclinical trials in Myotonic dystrophy in France (IV) prior to March 2025
  • 12 Mar 2025 Sanofi plans a BrAAVe phase I/II trial for Myotonic dystrophy (In children, In adolescence, In adults) in April 2025 (IV) (NCT06844214)

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