Research programme: RNA therapies - Apellis Pharmaceuticals
Latest Information Update: 01 Apr 2025
At a glance
- Originator Apellis Pharmaceuticals
- Class RNA
- Mechanism of Action Complement C3 expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Neurological disorders