Gene-edited FcRn therapy - Apellis Pharmaceuticals/Beam therapeutics
Latest Information Update: 01 Apr 2025
At a glance
- Originator Apellis Pharmaceuticals; Beam Therapeutics
- Class Gene therapies
- Mechanism of Action Gene modulators; Neonatal Fc receptor modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Unspecified
Most Recent Events
- 01 Apr 2025 Preclinical trials in Unspecified in USA (Parenteral) (Apellis Pharmaceutical pipeline; March 2025)