Research programme: secreted protein deficiency therapeutics - Metagenomi
Latest Information Update: 10 Apr 2025
At a glance
- Originator Metagenomi
- Class Gene therapies; Hepatoprotectants
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Liver disorders