GEN 6053
Alternative Names: GEN-6053Latest Information Update: 14 Jul 2025
At a glance
- Originator Suzhou GenAssist Therapeutics
- Class Gene therapies
- Mechanism of Action Dystrophin expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 02 Apr 2025 Preclinical trials in Duchenne muscular dystrophy in China (Parenteral), before April 2025 (GenAssist Therapeutics pipeline, April 2025)
- 02 May 2024 Suzhou GenAssist Therapeutics has a worldwide patent pending for 'gene editor for disease treatment and nucleic acid pharmaceutical composition for anti-fibrosis inhibitor'