DYNE 401
Alternative Names: DYNE-401Latest Information Update: 04 Apr 2025
At a glance
- Originator Dyne Therapeutics
- Class Enzymes
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Glycogen storage disease type II