Gene therapy targeting neuromuscular disease - Genkore
Latest Information Update: 29 May 2025
At a glance
- Originator GenKOre
- Class Gene therapies
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Neuromuscular disorders
Most Recent Events
- 26 Mar 2025 Early research in Neuromuscular disorders in South Korea (IV) prior to March 2025 (Genkore pipeline, March 20250