SNUG 01
Alternative Names: SNUG-01Latest Information Update: 30 May 2025
At a glance
- Originator SineuGene Therapeutics
- Developer Peking University Third Hospital; SineuGene Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; TRIM72 protein replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase 0 Amyotrophic lateral sclerosis
Most Recent Events
- 24 Mar 2025 US FDA approves IND application for SNUG 01 in Amyotrophic lateral sclerosis (ALS) (Intrathecal)
- 24 Mar 2025 SineuGene Therapeutics plans a phase I/IIa trial for Amyotrophic lateral sclerosis (ALS) (Intrathecal)
- 16 Sep 2024 Phase-0 for Amyotrophic lateral sclerosis in China (Intrathecal) (NCT06645197)